index - Thérapie génique pour la DMD & physiopathologie du muscle squelettique

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MES Exon skipping Muscles/physiopathology CD38 Autophagy CaV subunits DMO Muscular Dystrophy LncRNA Liver Long noncoding RNA Cachexia Dystrophin-EGFP Animals Mice LncARN Invivo Delivery Cardiomyopathy Inbred C57BL Becker muscular dystrophy BMD Multi resolution modeling Mitochondrial fission CTNNB1 Génomique Gene expression Genomic Muscular dystrophy Modificateurs de gènes Becker muscular dystrophy Base Sequence Drp1 Cell Line Dystrophin Male Dystrophie Musculaire de Duchenne DMD Knockout Muscle Muscle Strength Calcium NNOS Ex-vivo Dystrophie Musculaire de Becker BMD Cell homeostasis CaVβs Immunoglobulin Fc Fragments/pharmacology DHPR α1S L-Type DMD Metabolism Hepatocellular carcinoma Duchenne muscular dystrophy DMD MiARN LKB1 Inbred mdx Hear Human Umbilical Vein Endothelial Cells Energy Metabolism/drug effects Cells Calcium Channels Myogenesis Epigenetics Muscle Biology Diseases BMD Cardiomyopathie NAD+ Dystrophine Duchenne DMD dystrophy Inhibitors Allele‐specific silencing therapy Gene modifiers Centronuclear myopathy Multi exon skipping Cultured Long QT Mdx mouse Molecular Sequence Data Morphogenesis Skeletal muscle Clinical trials Dynamin 2 Cell Biology Gene Expression Regulation/drug effects Muscle development Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Humans Antisense oligonucleotides Becker BMD muscular dystrophy Homeostasis Dystrophin central domain Activin Receptors Animal/physiopathology Duchenne muscular dystrophy Multiresolution modeling Molecular docking Dystrophie musculaire de Becker Muscular Atrophy Myotendinous junction Dystrophy